Live Stream: Manifestations of Gaucher Disease: Rare or Under-recognized?
Live Virtual Symposium
Premiere Date: Thursday, February 23, 2023This activity offers CE credit for:
- ABIM (MOC)
- Medicine (accme)
- Nursing (ANCC)
- Pharmacy (acpe)
- PA (aapa)
- Other
All other clinicians will receive a Certificate of Attendance stating this activity was certified for AMA PRA Category 1 Credit™
Credit Expiration Date: Friday, February 23, 2024
Faculty
Tamanna Roshan Lal, MB, ChB, FAAP, FACMG (Moderator) Medical Geneticist Director of Clinical Trials Rare Disease Institute, Children's National Hospital Washington, DC |
Coy Heldermon, MD, PhD Associate Professor UFHealth Director of the Pediatric and Adult Multi-Disciplinary Lysosomal Storage Disease Clinics Gainesville, FL |
Dimitri Krainc, MD, PhD Chair, Department of Neurology Director, Simpson Querrey Center for Neurogenetics Aaron Montgomery Ward Professor Northwestern University Feinberg School of Medicine Chicago, IL |
Neal J. Weinreb, MD. FACP Voluntary Associate Professor Department of Human Genetics University of Miami Miller School of Medicine Miami, FL |
Statement of Need
Gaucher disease (GD) is a genetic disorder that causes fatty substances to accumulate to harmful levels in organs and tissues, often resulting in hepatosplenomegaly, anemia, thrombocytopenia, bone pain and fractures, and conditions like arthritis. GD is rare, and even specialists struggle to recognize and diagnose the condition. Delays to initiation of therapy are common and can result in irreversible complications.
During this 60-minute symposium live, expert panelists will discuss GD, including its less commonly reported manifestations, diagnostic pathways, and patient-centric multidisciplinary management of the disorder.
Learning Objectives
At the end of this CE activity, participants should be able to:
- Identify under-recognized clinical manifestations of GD.
- Evaluate the efficacy of current diagnostic methods in recognizing rare manifestations in GD.
- Implement patient-centric management strategies within a multidisciplinary team to optimize long-term outcomes of patients with GD.
Financial Support
Supported by an educational grant from Takeda Pharmaceuticals U.S.A., Inc.
Target Audience
Physicians, PAs, nurse practitioners, PCPs, nurses, pharmacists, genetic counselors, and pediatricians, specializing in hematology, neurology, hepatology, gastroenterology, pulmonologists, radiology, and orthopedic surgery.
Credit Information
ABIM MOC Credit:
Successful completion of this CME activity, which includes participation in the evaluation component, enables the participant to earn up to 1.0 medical knowledge MOC points in the American Board of Internal Medicine's (ABIM) Maintenance of Certification (MOC) program. Participants will earn MOC points equivalent to the amount of CME credits claimed for the activity. It is the CME activity provider's responsibility to submit participant completion information to ACCME for the purpose of granting ABIM MOC credit.
Learning Formats
Live activity
Royal College MOC:
Through an agreement between the Accreditation Council for Continuing Medical Education and the Royal College of Physicians and Surgeons of Canada, medical practitioners participating in the Royal College MOC Program may record completion of accredited activities registered under the ACCME’s “CME in Support of MOC” program in Section 3 of the Royal College’s MOC Program.
MIPS Improvement Activity:
This activity counts towards MIPS Improvement Activity requirements under the Medicare Access and CHIP Reauthorization Act of 2015 (MACRA). Clinicians should submit their improvement activities by attestation via the CMS Quality Payment Program website.
Eligibility: Registration for WORLDSymposium 2023 and an official name badge are required to attend this satellite symposium.
It is the policy of CME Outfitters, LLC, to ensure independence, balance, objectivity, and scientific rigor and integrity in all of their CE activities. Faculty must disclose to the participants any relationships with commercial companies whose products or devices may be mentioned in faculty presentations, or with the commercial supporter of this CE activity. CME Outfitters, LLC, has evaluated, identified, and mitigated any potential conflicts of interest through a rigorous content validation procedure, use of evidence-based data/research, and a multidisciplinary peer review process. The following information is for participant information only. It is not assumed that these relationships will have a negative impact on the presentations.
Dr. Roshan Lal reports the following financial relationships:
Advisory Board: Takeda Pharmaceuticals U.S.A., Inc. (Gaucher Advisory Board)
Consultant: FDNA INC.
Speakers Bureau: BioMarin (PKU)
Dr. Heldermon reports the following financial relationships:
Advisory Board: Chiesi USA, Inc.; Orphazyme; REGENXBIO Inc.; and Sanofi
Consultant: Atheneum; Cardinal Health; Curio Science; Guidepoint Global; IntrinsiQ Specialty Solutions; Reckner Healthcare; Sage Research; Sanofi; Targeted Oncology; and Third Bridge Consulting
Stock Shareholder (ownership Interest): Lacerta Therapeutics
Dr. Krainc reports no financial relationships to disclose.
Dr. Weinreb reports the following financial relationships:
Advisory Board: AVROBIO, Inc. (Disease Monitoring Safety Board); Pfizer Inc. (Medical Advisory Board for the Taliglucerase alfa Gaucher Registry); Sanofi (Scientific Advisory Board for the International Collaborative Gaucher Group (ICGG) Gaucher Registry); and Takeda Pharmaceuticals U.S.A., Inc. (Medical Advisory Board for Gaucher Disease)
Consultant: Pfizer Inc. and Sanofi
Speakers Bureau: Sanofi
The following peer reviewer and CME Outfitters staff have no financial relationships:
Faculty of this CE activity may include discussions of products or devices that are not currently labeled for use by the FDA. The faculty have been informed of their responsibility to disclose to the audience if they will be discussing off-label or investigational uses (any uses not approved by the FDA) of products or devices.
Questions about this activity? Call us at 877.CME.PROS (877.263.7767).
This document was last modified on:
MMS-129-022323-20